EFF Fall 2020 Program

EFF Fall 2020 Program

This was the exciting program of the Fall EFF Summit which took place in September 2020. We'll share the program for our next event when it becomes available. If you want us to keep you posted, subscribe to our newsletter.

Webinar recording

Did you miss the webinar? No worries, we have a full recording with captions right here. If you want to skip to a part that is of interest to you, then please open the video in YouTube and use the links in the description to navigate through the video.

The presented slides are available here: download presentation (PDF). Please also check out the complementary videos in the program below.

Timetable - Wednesday 23 September 2020

Welcome to the webinar

Presented by: Daniel de Boer, CEO, ProQR Therapeutics

Daniel de Boer, the CEO of ProQR opened the Fall EFF Summit by giving a short introduction of ProQR and the status of ProQR.
He speaks about how ProQR has done since our last conference last February and how COVID-19 has impacted to our daily work.

Sepofarsen update

Presented by: Aniz Girach, Chief Medical Officer, ProQR Therapeutics

Aniz Girach gave a short update on the success to date and latest findings of the sepofarsen program for LCA, and then started the interactive sessions.

A more elaborate presentation on the Sepofarsen InSight phase 1/2 extension study with Aniz Girach and Dr. MacDonald is available in the Expert Perspectives Call below, that was recorded on July 20, 2020.

Live Q&A on LCA and sepofarsen

Dr. Ian M. MacDonald & Dr. Aniz Girach, moderated by Jessica Ibbitson

This Q&A session with Dr. Ian MacDonald and Dr. Aniz Girach took 25 minutes. They answered audience questions about Leber congenital amaurosis 10 and the sepofarsen data.

Panel discussion on patient’s perspective on clinical research.

Panelists: Francesca Diodati, Ian MacDonald & Aniz Girach, moderator: Jessica Ibbitson

To finalize the Fall EFF Summit, we gave the audience the chance to ask our panelists questions about a topic we greatly care about: 'patient's perspective on clinical research'.

We strongly recommend watching the ProQR talks episode #2 as an introduction to this session.

Close out

Speaker: Aniz Girach

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